What are the goals and activities of the Center?Our goal is to be a world leader in providing solutions to childhood diseases. Our approach is to combine outstanding basic research with innovative technologies to translate discoveries into clinical benefits.
We emphasize developmental biology and have core strengths in stem cells and developmental biology to help us to understand what goes wrong in children with inherited diseases and provide us with insights into regeneration and replacement of defective organs and tissues.
We employ a multi-disciplinary strategy to assemble complementary talents and focus them on solving problems in childhood health. Our team includes expertise in genetically tractable model organisms and chemical biology approaches to identifying chemicals that modulate drug targets, thus setting the stage for production of innovative new therapeutics.
Working together, and with our collaborative partners, our mission is to provide breakthroughs in medical research that lead to cures for life threatening diseases of children.